Study Rationale: Core funding programs at The Michael J. Fox Foundation (MJFF) have historically focused on research to understand, measure, and treat Parkinson’s disease (PD). MJFF is now seeking to expand its research agenda to examine pathways for evaluating and enhancing access to future, innovative PD treatments. Pilots to evaluate “where to play” are ongoing, but a long-term plan and strategic vision have not been established. MJFF now seeks support developing a forward-looking strategic roadmap, with specific focus on an integrated approach centered on collection and use of real world data and evidence to improve access to and investments in PD therapies.
Hypothesis: We hypothesize that our approach will identify potential opportunities for MJFF to add value in preparing for innovative PD treatment evaluation and access.
Study Design: We will first identify key landscape trends and drivers/barriers to bringing new, innovative treatments to market in the next five to ten years. We will then characterize existing value frameworks and analog indications to understand potential approaches to addressing market access challenges in PD. Lastly, we will facilitate alignment on comprehensive list of potential opportunities for MJFF to add value in preparing for innovative PD treatment evaluation and access.
Impact on Diagnosis/Treatment of Parkinson’s disease: This project will identify and prioritize potential initiatives for MJFF investment to improve perception, evaluation and market access for innovative future therapies for PD.
Next Steps for Development: The next steps of this project would be to develop a roadmap for implementing the priority initiatives, whether it’s engaging payers or generating new evidence to demonstrate clinical and pharmacoeconomic value.